Sma News & Perspectives

We discuss how Risdiplam improves survival and motor functions in infants with Type 1 SMA. Also, Columnist Michael Casten reflects on his daughter's ninth birthday, and how far she's come since her initial SMA diagnosis. Are you interested in understanding gene therapy? ExploreGeneTherapy.com has helpful information about gene therapy, including its history and how it is being investigated for the treatment of genetic diseases. Visit www.exploregenetherapy.com